SILVER SPRING, Md., Dec. 13, 2024 /PRNewswire/ -- Today, the U.S. Food and Drug Administration approved Crenessity (crinecerfont) to be used together with glucocorticoids (steroids) to control androgen (a testosterone-like hormone) levels in adults and pediatric patients 4 years of age and older with classic congenital adrenal hyperplasia (CAH).
"Today's approval provides an important advance for patients with classic congenital adrenal hyperplasia and highlights the FDA's continued commitment to advancing effective and safe treatments for rare diseases," said Theresa Kehoe M.D., director of the Division of General Endocrinology in the FDA's Center for Drug Evaluation and Research. "The FDA will continue working with patients, drug companies and health care providers to address the unmet medical needs of the rare disease community."
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